How could you design a gene therapy to "cure" Huntingtos disease and Lesh-Nyhan in effected people?...
Homework Answers
Lesh -Nyhan disease is caused due to mutation of HPRT gene that produces the enzyme hypoxanthine-guanine phosphoribosyltransferase (HGPRT) and the gene therapy can be designed to correct the mutation of the HPRT gene thus helping in reducing away the enzyme deficiency
In case of Huntingtos disease ,the gene therapy can be designed to limit the production of the toxic huntington protein.Production of less toxic protein in the brain would lead to a slower breakdown of neurons.
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could you design a gene therapy to "cure" Huntingtos disease and
Lesh-Nyhan in effected people?...
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How Speech Therapy might help people with Parkinson disease ?
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genetics help please
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